Final Report - NEUGENE (Advanced gene therapy tools for treatment of CNS-specific disorders)
Project ID: 222925Funded under: FP7-HEALTH
This is the publishable summary report for the NEUGENE project which received funding under the European Commission's Seventh Framework Programme (FP7). NEUGENE's mainly objectives were to develop and to validate the tools necessary for safe, efficient, durable, targeted and regulated expression of therapeutic molecules within the Central nervous system (CNS). In order to ensure safety and longevity of vectors, the consortium focused on both LV and AAV vectors, which have already demonstrated the ability to mediate long-lasting and stable transgene expression in CNS. These vectors were significantly improved through work described in the respective WPs, resulting in gene therapy vectors applicable to CNS disorders as defined by the call.
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Record Number: 13859 / Last updated on: 2011-04-14