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Preclinical development of a nanomedicine candidate for Fabry rare disease treatment to enter clinical phase

CORDIS provides links to public deliverables and publications of HORIZON projects.

Links to deliverables and publications from FP7 projects, as well as links to some specific result types such as dataset and software, are dynamically retrieved from OpenAIRE .

Publications

Targeted nanoliposomes to improve enzyme replacement therapy of Fabry disease (opens in new window)

Author(s): Judit Tomsen-Melero, Marc Moltó-Abad, Josep Merlo-Mas, Zamira V. Díaz-Riascos, Edgar Cristóbal-Lecina, Andreu Soldevila, Thomas Altendorfer-Kroath, Dganit Danino, Inbal Ionita, Jan Skov Pedersen, Lyndsey Snelling, Hazel Clay, Aida Carreño, José L. Corchero, Daniel Pulido, Josefina Casas, Jaume Veciana, null Simó Schwartz Jr., Santi Sala, Albert Font, Thomas Birngruber, Miriam Royo, Alba Córdoba, Nora Ventosa, Ibane Abasolo, Elisabet González-Mira
Published in: Science Advances, Issue 10, 2024, ISSN 2375-2548
Publisher: American Association for the Advancement of Science (AAAS)
DOI: 10.1126/sciadv.adq4738

Nanovesicles (opens in new window)

Author(s): N. Pujol-Solé, L. Ferrer-Tasies, J. Tomsen-Melero, A. Carreño, C. Castellar-Álvarez, M. Alcaina-Hernando, N. Ventosa, E. González-Mira, M. Köber
Published in: Characterisation of Drug Nanocarriers, 2024
Publisher: Royal Society of Chemistry
DOI: 10.1039/9781837672981-00120

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