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Late Clinical Development of KH176: an innovative orphan drug to reach mitochondrial disease patients & market

Deliverables

Dissemination material

Dissemination material

Press releases and information papers on KHON2bTREAT to relevant stakeholders

Press releases and information papers on KHON2bTREAT to relevant stakeholders

Publications

Sonlicromanol improves neuronal network dysfunction and transcriptome changes linked to m.3243A>G heteroplasmy in iPSC-derived neurons

Author(s): Teun M. Klein Gunnewiek Anouk H.A. Verboven Iris Pelgrim Mark Hogeweg Chantal Schoenmaker Herma Renkema Julien Beyrath Jan Smeitink Bert B.A. de Vries Peter-Bram A.C. ’t Hoen Tamas Kozicz Nael Nadif Kasri
Published in: ISSCR, Issue Volume 16, Issue 9, 2021, Page(s) 2197-2212, ISSN 0020-0255
Publisher: Elsevier BV
DOI: 10.1016/j.stemcr.2021.07.002

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