Third-generation lentiviral gene therapy rescues function in a mouse model of Usher 1B
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Author(s):
Juliane W Schott, Peixin Huang, Michael Morgan, Jennifer Nelson-Brantley, Ally Koehler, Bryan Renslo, Hildegard Büning, Athanasia Warnecke, Axel Schambach, Hinrich Staecker
Published in:
Molecular Therapy, 2023, ISSN 1525-0024
Publisher:
Cell Press
DOI:
10.1016/j.ymthe.2023.10.018
Molecular Therapy - Nucleic Acids
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Author(s):
Larissa Nassauer, Hinrich Staecker, Peixin Huang, Bryan Renslo, Madeleine Goblet, Jennifer Harre, Athanasia Warnecke, Juliane W Schott, Michael Morgan, Melanie Galla, Axel Schambach
Published in:
Molecular Therapy Nucleic Acids, 2024, ISSN 2162-2531
Publisher:
Nature Publishing Group
DOI:
10.1016/j.omtn.2024.102157