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CONSORTIUM FOR DEVELOPING REGULATORY CAPACITY FOR CLINICAL TRIALS USING GENE THERAPY PRODUCTS AND STRENGTHENING PHARMACOVIGILANCE IN THE CONDUCT OF CLINICAL TRIALS IN EAST AFRICA

CORDIS provides links to public deliverables and publications of HORIZON projects.

Links to deliverables and publications from FP7 projects, as well as links to some specific result types such as dataset and software, are dynamically retrieved from OpenAIRE .

Publications

Progression of biological markers in spinocerebellar ataxia type 3: longitudinal analysis of prospective data from the ESMI cohort (opens in new window)

Author(s): Moritz Berger; Hector Garcia-Moreno; Mónica Ferreira; Jeannette Hubener-Schmid; Tamara Schaprian; Philipp Wegner; Tim Elter; Kennet M. Teichmann; Magda M. Santana; Marcus Grobe-Einsler; Demet Oender; Berkan S.C. Koyak; Sarah Bernsen; Luís Pereira de Almeida; Patrick Silva; Joana Afonso Ribeiro; Inês Cunha; Cristina Gonzalez-Robles; Shamsher Khan; Amanda Heslegrave; Henrik Zetterberg; Manuela Lima; Mafalda Raposo; Ana F. Ferreira; João Vasconcelos; Bart P. van de Warrenburg; Judith van Gaalen; Teije H. van Prooije; Jeroen de Vries; Ludger Schols; Olaf Riess; Matthis Synofzik; Dagmar Timmann; Andreas Thieme; Friedrich Erdlenbruch; Jon Infante; Ana L. Pelayo-Negro; Leire Manrique; Kathrin Reetz; Imis Dogan; Gulin Oz; James M. Joers; Khalafalla Bushara; Chiadikaobi Onyike; Michal Povazan; Heike Jacobi; Jeremy D. Schmahmann; Eva-Maria Ratai; Matthias Schmid; Paola Giunti; Thomas Klockgether; Jennifer Faber
Published in: The Lancet Regional Health - Europe, Issue 55, 2025, ISSN 2666-7762
Publisher: Elsevier Ltd
DOI: 10.1016/J.LANEPE.2025.101339

Circadian rhythms are disrupted in patients and preclinical models of Machado-Joseph disease (opens in new window)

Author(s): Rodrigo F N Ribeiro, Dina Pereira, Sara M Lopes, Tiago Reis, Patrick Silva, Diana D Lobo, Laetitia S Gaspar, João Durães, Ana Rita Fernandes, Marisa Ferreira-Marques, Catarina Carvalhas-Almeida, João Peça, Ana Rita Álvaro, Isabel Santana, Magda M Santana, Maria Manuel C Silva, Luís Pereira de Almeida, Cláudia Cavadas
Published in: Brain, Issue 148, 2025, ISSN 0006-8950
Publisher: Oxford University Press (OUP)
DOI: 10.1093/BRAIN/AWAF199

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