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CORDIS - Forschungsergebnisse der EU
CORDIS

CONSORTIUM FOR DEVELOPING REGULATORY CAPACITY FOR CLINICAL TRIALS USING GENE THERAPY PRODUCTS AND STRENGTHENING PHARMACOVIGILANCE IN THE CONDUCT OF CLINICAL TRIALS IN EAST AFRICA

CORDIS bietet Links zu öffentlichen Ergebnissen und Veröffentlichungen von HORIZONT-Projekten.

Links zu Ergebnissen und Veröffentlichungen von RP7-Projekten sowie Links zu einigen Typen spezifischer Ergebnisse wie Datensätzen und Software werden dynamisch von OpenAIRE abgerufen.

Leistungen

Project launch report (öffnet in neuem Fenster)

Project Launch meeting. Launch of the project website.

Obtaining ethical approval of the proposed study (öffnet in neuem Fenster)

Submission for ethical approval s and administrative clearance

Researchers, Clinicians & NRA personnel sensitized and trained on aspects of research using gene therapy products. (öffnet in neuem Fenster)

Workshops, webinars and stakeholders meetings

Plan for the exploitation and dissemination of results including communication activities (öffnet in neuem Fenster)

Exploitation and dissemination Plan

Short term trainings on PV in Clinical Trials (öffnet in neuem Fenster)

Enrol 5 members from NDA and UNCST in medium- and short-term trainings on Pharmacovigilance delivered Eu2p consortium

Results Framework (öffnet in neuem Fenster)

Monitoring and evaluation Framework for the grant implementation process

Set up of Project website and other publicity materials such as (flyers, posters, brochures) (öffnet in neuem Fenster)

Sent up of Project information on institutional website and making project publicity Materials to share with colleagues and associations the grant and activities

Data management plan (öffnet in neuem Fenster)

Development of the Data Management Plan, this also provides details on how data from the grant will be disseminated.

Veröffentlichungen

Progression of biological markers in spinocerebellar ataxia type 3: longitudinal analysis of prospective data from the ESMI cohort (öffnet in neuem Fenster)

Autoren: Moritz Berger; Hector Garcia-Moreno; Mónica Ferreira; Jeannette Hubener-Schmid; Tamara Schaprian; Philipp Wegner; Tim Elter; Kennet M. Teichmann; Magda M. Santana; Marcus Grobe-Einsler; Demet Oender; Berkan S.C. Koyak; Sarah Bernsen; Luís Pereira de Almeida; Patrick Silva; Joana Afonso Ribeiro; Inês Cunha; Cristina Gonzalez-Robles; Shamsher Khan; Amanda Heslegrave; Henrik Zetterberg; Manuela Lima; Mafalda Raposo; Ana F. Ferreira; João Vasconcelos; Bart P. van de Warrenburg; Judith van Gaalen; Teije H. van Prooije; Jeroen de Vries; Ludger Schols; Olaf Riess; Matthis Synofzik; Dagmar Timmann; Andreas Thieme; Friedrich Erdlenbruch; Jon Infante; Ana L. Pelayo-Negro; Leire Manrique; Kathrin Reetz; Imis Dogan; Gulin Oz; James M. Joers; Khalafalla Bushara; Chiadikaobi Onyike; Michal Povazan; Heike Jacobi; Jeremy D. Schmahmann; Eva-Maria Ratai; Matthias Schmid; Paola Giunti; Thomas Klockgether; Jennifer Faber
Veröffentlicht in: The Lancet Regional Health - Europe, Ausgabe 55, 2025, ISSN 2666-7762
Herausgeber: Elsevier Ltd
DOI: 10.1016/J.LANEPE.2025.101339

Circadian rhythms are disrupted in patients and preclinical models of Machado-Joseph disease (öffnet in neuem Fenster)

Autoren: Rodrigo F N Ribeiro, Dina Pereira, Sara M Lopes, Tiago Reis, Patrick Silva, Diana D Lobo, Laetitia S Gaspar, João Durães, Ana Rita Fernandes, Marisa Ferreira-Marques, Catarina Carvalhas-Almeida, João Peça, Ana Rita Álvaro, Isabel Santana, Magda M Santana, Maria Manuel C Silva, Luís Pereira de Almeida, Cláudia Cavadas
Veröffentlicht in: Brain, Ausgabe 148, 2025, ISSN 0006-8950
Herausgeber: Oxford University Press (OUP)
DOI: 10.1093/BRAIN/AWAF199

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