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First Targeted Therapy to FIGHT Hemophagocytic Lymphohistiocytosis (HLH): A novel approach to HLH

CORDIS fournit des liens vers les livrables publics et les publications des projets HORIZON.

Les liens vers les livrables et les publications des projets du 7e PC, ainsi que les liens vers certains types de résultats spécifiques tels que les jeux de données et les logiciels, sont récupérés dynamiquement sur OpenAIRE .

Publications

IFNɣ Block, Treosulfan Conditioning and αβ T Cell Deplete PBSCT for XIAP-Deficient HLH

Auteurs: Ciara O’Rafferty; Mark Velangi; Sarah Lawson; Prashant Hiwarkar; Jayashree Motwani
Publié dans: Springer Science and Business Media LLCJournal of Clinical Immunology 2017
Identifiant permanent: Digital Object Identifier:10.1007/s10875-017-0413-7; Microsoft Academic Graph Identifier:2655426445

The interferon-gamma pathway is selectively up-regulated in the liver of patients with secondary hemophagocytic lymphohistiocytosis

Auteurs: Giusi Prencipe; Claudia Bracaglia; Ivan Caiello; Antonia Pascarella; Paola Francalanci; Manuela Pardeo; Alessandra Meneghel; Giorgia Martini; Marianna N. Rossi; Antonella Insalaco; Giulia Marucci; Valerio Nobili; Marco Spada; Francesco Zulian; Fabrizio De Benedetti
Publié dans: Public Library of Science (PLoS)PLoS ONE, Vol 14, Iss 12, p e0226043 (2019) 2019
Identifiant permanent: Digital Object Identifier:10.1371/journal.pone.0226043; PubMed ID:31846457; PubMed Central ID:PMC6917341; Microsoft Academic Graph Identifier:2995649581; Handle:11390/1273729

Inhibitory 2B4 contributes to NK cell education and immunological derangements in XLP1 patients

Auteurs: Paolo Canevali; Maurizio Aricò; Cristina Bottino; Cristina Bottino; Michela Falco; Francesca Bellora; Claudia Tuberosa; Fabrizio Loiacono; Concetta Micalizzi; Maria Cristina Mingari; Stefania Marcenaro; Daniela Pende; Raffaella Meazza; Alessandro Moretta; Lorenzo Moretta; Franco Locatelli
Publié dans: WileyCrossref 2017
Identifiant permanent: Digital Object Identifier:10.1002/eji.201646885; PubMed ID:28386908; Microsoft Academic Graph Identifier:2605335384; Handle:10807/230030; Handle:11573/1479849; Handle:11567/888019

Macrophage Activation Syndrome: different mechanisms leading to a one clinical syndrome

Auteurs: Claudia Bracaglia; Giusi Prencipe; Fabrizio De Benedetti
Publié dans: Springer Science and Business Media LLCPediatr Rheumatol Online J 2017
Identifiant permanent: Digital Object Identifier:10.1186/s12969-016-0130-4; PubMed ID:28095869; PubMed Central ID:PMC5240371; Microsoft Academic Graph Identifier:2574674925

Elevated circulating levels of interferon-γ and interferon-γ-induced chemokines characterise patients with macrophage activation syndrome complicating systemic juvenile idiopathic arthritis

Auteurs: Bracaglia, Claudia; de Graaf, Kathy; Pires Marafon, Denise; Guilhot, Florence; Ferlin, Walter; Prencipe, Giusi; Caiello, Ivan; Davì, Sergio; Schulert, Grant; Ravelli, Angelo; Grom, Alexei A; de Min, Cristina; De Benedetti, Fabrizio
Publié dans: Elsevier BVAnnals of the Rheumatic Diseases 2017
Identifiant permanent: Digital Object Identifier:10.1136/annrheumdis-2015-209020; PubMed ID:27296321; Microsoft Academic Graph Identifier:2444247510; Handle:11567/936031

XLP1 inhibitory effect by 2B4 does not affect DNAM‐1 and NKG2D activating pathways in NK cells

Auteurs: Valentina Cetica; Cristina Bottino; Cristina Bottino; Michela Falco; Raffaella Meazza; Claudia Tuberosa; Silvia Parolini; Alessandro Moretta; Concetta Micalizzi; Maria Cristina Mingari; Maurizio Aricò; Lorenzo Moretta; Daniela Pende; Fabrizio Loiacono
Publié dans: WileyEuropean Journal of Immunology; Vol 44 2014
Identifiant permanent: Digital Object Identifier:10.1002/eji.201344312; PubMed ID:24496997; Microsoft Academic Graph Identifier:1586530170; Handle:11379/453137; Handle:11567/700170

Patients with Griscelli syndrome and normal pigmentation identify RAB27A mutations that selectively disrupt MUNC13-4 binding

Auteurs: Valentina Cetica; Yvonne Hackmann; Samantha Grieve; Elena Sieni; Benedetta Ciambotti; Maria Luisa Coniglio; Daniela Pende; Kimberly Gilmour; ROMAGNOLI, PAOLO; Gillian M. Griffiths; Maurizio Aricò
Publié dans: Elsevier BVJ Allergy Clin Immunol 2015
Identifiant permanent: Digital Object Identifier:10.1016/j.jaci.2014.08.039; Digital Object Identifier:10.17863/cam.23879; PubMed ID:25312756; PubMed Central ID:PMC4418747; Microsoft Academic Graph Identifier:2036855076; Handle:2158/903930

Genetic predisposition to hemophagocytic lymphohistiocytosis: Report on 500 patients from the Italian registry

Auteurs: Cetica, Valentina; Sieni, Elena; Pende, Daniela; Danesino, Cesare; De Fusco, Carmen; Locatelli, Franco; Micalizzi, Concetta; Putti, Maria Caterina; Biondi, Andrea; Fagioli, Franca; Moretta, Lorenzo; Griffiths, Gillian M.; Luzzatto, Lucio; Aricò, Maurizio
Publié dans: Elsevier BVJ Allergy Clin Immunol 2016
Identifiant permanent: Digital Object Identifier:10.1016/j.jaci.2015.06.048; PubMed ID:26342526; PubMed Central ID:PMC4699615; Microsoft Academic Graph Identifier:1502651188; Handle:10281/97365; Handle:10807/228778; Handle:11573/1487549; Handle:2318/1690476; Handle:11571/1112743

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