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Gene therapy of inherited retinal diseases

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Seeing the Light after 25 Years of Retinal Gene Therapy

Author(s): Ivana Trapani, Alberto Auricchio
Published in: Trends in Molecular Medicine, Issue 24/8, 2018, Page(s) 669-681, ISSN 1471-4914
DOI: 10.1016/j.molmed.2018.06.006

High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction In Vitro and in Mouse Retina

Author(s): Andrea Maddalena, Fabio Dell'Aquila, Pia Giovannelli, Paola Tiberi, Luca Giorgio Wanderlingh, Sandro Montefusco, Patrizia Tornabene, Carolina Iodice, Feliciano Visconte, Annamaria Carissimo, Diego Luis Medina, Gabriella Castoria, Alberto Auricchio
Published in: Human Gene Therapy, Issue 29/8, 2018, Page(s) 886-901, ISSN 1043-0342
DOI: 10.1089/hum.2017.220

Triple Vectors Expand AAV Transfer Capacity in the Retina

Author(s): Andrea Maddalena, Patrizia Tornabene, Paola Tiberi, Renato Minopoli, Anna Manfredi, Margherita Mutarelli, Settimio Rossi, Francesca Simonelli, Jurgen K. Naggert, Davide Cacchiarelli, Alberto Auricchio
Published in: Molecular Therapy, Issue 26/2, 2018, Page(s) 524-541, ISSN 1525-0016
DOI: 10.1016/j.ymthe.2017.11.019

Has retinal gene therapy come of age? From bench to bedside and back to bench

Author(s): Ivana Trapani, Alberto Auricchio
Published in: Human Molecular Genetics, 2019, ISSN 0964-6906
DOI: 10.1093/hmg/ddz130