When repetita no-longer iuvant: somatic instability of the CAG triplet in Huntington’s disease
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Autores:
Elena Cattaneo, Davide Scalzo, Martina Zobel, Raffaele Iennaco, Camilla Maffezzini, Dario Besusso, Simone Maestri
Publicado en:
Nucleic Acids Research, Edición 53, 2025, ISSN 0305-1048
Editor:
Oxford University Press
DOI:
10.1093/nar/gkae1204
Huntington’s disease cellular phenotypes are rescued non-cell autonomously by healthy cells in mosaic telencephalic organoids
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Autores:
Maura Galimberti, Maria R. Nucera, Vittoria D. Bocchi, Paola Conforti, Elena Vezzoli, Matteo Cereda, Camilla Maffezzini, Raffaele Iennaco, Andrea Scolz, Andrea Falqui, Chiara Cordiglieri, Martina Cremona, Ira Espuny-Camacho, Andrea Faedo, Dan P. Felsenfeld, Thomas F. Vogt, Valeria Ranzani, Chiara Zuccato, Dario Besusso, Elena Cattaneo
Publicado en:
Nature Communications, Edición 15, 2024, ISSN 2041-1723
Editor:
Nature Publishing Group
DOI:
10.1038/s41467-024-50877-x