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Therapeutic Allele Engineering: A novel technology for cell therapy

Publications

Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapy

Author(s): Romina Marone; Emmanuelle Landmann; Anna Devaux; Rosalba Lepore; Denis Seyres; Jessica Zuin; Thomas Burgold; Corinne Engdahl; Giuseppina Capoferri; Alessandro Dell’Aglio; Clément Larrue; Federico Simonetta; Julia Rositzka; Manuel Rhiel; Geoffroy Andrieux; Danielle N. Gallagher; Markus S. Schröder; Amélie Wiederkehr; Alessandro Sinopoli; Valentin Do Sacramento; Anna Haydn; Laura Garcia-Prat; C
Published in: Journal of Experimental Medicine, 220 (12), Issue 4, 2023, ISSN 0022-1007
Publisher: Rockefeller University Press
DOI: 10.1084/jem.20231235

Forced expression of the non-coding RNA miR-17∼92 restores activation and function in CD28-deficient CD4+ T cells

Author(s): Marianne Dölz; Marko Hasiuk; John D. Gagnon; Mara Kornete; Romina Marone; Glenn Bantug; Robin Kageyama; Christoph Hess; K. Mark Ansel; Denis Seyres; Julien Roux; Lukas T. Jeker
Published in: iScience, Issue 1, 2022, ISSN 2589-0042
Publisher: Cell Press, Elsevier Inc.
DOI: 10.1016/j.isci.2022.105372

Deletion of SNX9 alleviates CD8 T cell exhaustion for effective cellular cancer immunotherapy

Author(s): Marcel P. Trefny; Nicole Kirchhammer; Priska Auf der Maur; Marina Natoli; Dominic Schmid; Markus Germann; Laura Fernandez Rodriguez; Petra Herzig; Jonas Lötscher; Maryam Akrami; Jane C. Stinchcombe; Michal A. Stanczak; Andreas Zingg; Melanie Buchi; Julien Roux; Romina Marone; Leyla Don; Didier Lardinois; Mark Wiese; Lukas T. Jeker; Mohamed Bentires-Alj; Jérémie Rossy; Daniela S. Thommen; Gillia
Published in: Nature Communications, Issue 3, 2023, ISSN 2041-1723
Publisher: Nature Publishing Group
DOI: 10.1038/s41467-022-35583-w

T helper cells exhibit a dynamic and reversible 3’UTR landscape

Author(s): Denis Seyres; Oliver Gorka; Ralf Schmidt; Romina Marone; Mihaela Zavolan; Lukas T. Jeker
Published in: RNA Journal, Issue 1, 2024, ISSN 1469-9001
Publisher: Cold Spring Harbor Laboratory
DOI: 10.1101/2023.01.19.523753

Leveraging microRNAs for cellular therapy

Author(s): Marko Hasiuk; Marianne Dölz; Romina Marone; Lukas T. Jeker
Published in: Immunology Letters, Issue 2, 2023, ISSN 0165-2478
Publisher: Elsevier BV
DOI: 10.1016/j.imlet.2023.08.005

CRISPR/Cas-based Human T cell Engineering: Basic Research and Clinical Application

Author(s): Bettina E Bernard, Emmanuelle Landmann, Lukas T Jeker, Kathrin Schumann
Published in: Immunology Letters, 2022, ISSN 0165-2478
Publisher: Elsevier BV
DOI: 10.1016/j.imlet.2022.03.005

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