Deliverables Other (1) A suite of branded template material and a website A suite of branded template material and a website for dissemination and public awareness of the HIT-CF project Publications Peer reviewed articles (8) Responsible use of organoids in precision medicine: the need for active participant involvement Author(s): Michael A. Lensink, Karin R. Jongsma, Sarah N. Boers, Jacquelien J. Noordhoek, Jeffrey M. Beekman, Annelien L. Bredenoord Published in: Development, Issue 147/7, 2020, ISSN 0950-1991 Publisher: The Company of Biologists Ltd. DOI: 10.1242/dev.177972 Organoids for personalized treatment of Cystic Fibrosis: Professional perspectives on the ethics and governance of organoid biobanking Author(s): Michael A. Lensink, Sarah N. Boers, Karin R. Jongsma, Sarah E. Carter, Cornelis K. van der Ent, Annelien L. Bredenoord Published in: Journal of Cystic Fibrosis, Issue 20/3, 2021, Page(s) 443-451, ISSN 1569-1993 Publisher: Elsevier BV DOI: 10.1016/j.jcf.2020.11.015 Organoids as a personalized medicine tool for ultra-rare mutations in cystic fibrosis: The case of S955P and 1717-2A>G Author(s): Iris A.L. Silva, Tereza Doušová, Sofia Ramalho, Raquel Centeio, Luka A. Clarke, Violeta Railean, Hugo M. Botelho, Andrea Holubová, Iveta Valášková, Jiunn-Tyng Yeh, Tzyh-Chang Hwang, Carlos M. Farinha, Karl Kunzelmann, Margarida D. Amaral Published in: Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease, Issue 1866/11, 2020, Page(s) 165905, ISSN 0925-4439 Publisher: Elsevier BV DOI: 10.1016/j.bbadis.2020.165905 Intestinal organoids to model cystic fibrosis Author(s): Peter van Mourik, Jeffrey M. Beekman, Cornelis K. van der Ent Published in: European Respiratory Journal, Issue 54/1, 2019, Page(s) 1802379, ISSN 0903-1936 Publisher: European Respiratory Society DOI: 10.1183/13993003.02379-2018 Protocol for Application, Standardization and Validation of the Forskolin-Induced Swelling Assay in Cystic Fibrosis Human Colon Organoids Author(s): Annelotte M. Vonk, Peter van Mourik, Anabela S. Ramalho, Iris A.L. Silva, Marvin Statia, Evelien Kruisselbrink, Sylvia W.F. Suen, Johanna F. Dekkers, Frank P. Vleggaar, Roderick H.J. Houwen, Jasper Mullenders, Sylvia F. Boj, Robert Vries, Margarida D. Amaral, Kris de Boeck, Cornelis K. van der Ent, Jeffrey M. Beekman Published in: STAR Protocols, Issue 1/1, 2020, Page(s) 100019, ISSN 2666-1667 Publisher: Cell Press DOI: 10.1016/j.xpro.2020.100019 Extensive CFTR sequencing through NGS in Brazilian individuals with cystic fibrosis: unravelling regional discrepancies in the country Author(s): Luiz Vicente Ribeiro Ferreira da Silva Filho, Paulo José Cauduro Maróstica, Rodrigo Abensur Athanazio, Francisco José Caldeira Reis, Neiva Damaceno, Angela Tavares Paes, Adilson Yuuji Hira, David Schlesinger, Fernando Kok, Margarida D. Amaral, Mara Lícia Machado Antunes, Lilian Cristina Ferreira Andries, Virginia Auxiliadora Freitas de Castro, Fabíola Villac Adde, Maria Fernanda Botelho Herna Published in: Journal of Cystic Fibrosis, Issue 20/3, 2021, Page(s) 473-484, ISSN 1569-1993 Publisher: Elsevier BV DOI: 10.1016/j.jcf.2020.08.007 Rationale and design of the HIT-CF organoid study: stratifying cystic fibrosis patients based on intestinal organoid response to different CFTR-modulators Author(s): Peter van Mourik, Sabine Michel, Annelotte M. Vonk, Jeffrey M. Beekman, Cornelis K. van der Ent, Hilde De Keyser, Elise Lammertyn, Silke van Koningsbruggen-Rietschel, Lutz Naehrlich, Judith Pool, Marc van de Craen, Begoña Aguilera, Johanna Pott, Rob G. J. Vries, Sylvia F. Boj, Kris De Boeck, François Vermeulen, Anabela S. Ramalho, Iris A. L. Silva, Margarida D. Amaral, Matthew Goddeeris, Geoffre Published in: Translational Medicine Communications, Issue 5/1, 2020, ISSN 2396-832X Publisher: BMC - part of springer Nature DOI: 10.1186/s41231-020-00060-3 Personalized Medicine Based on Nasal Epithelial Cells: Comparative Studies with Rectal Biopsies and Intestinal Organoids Author(s): Iris A. L. Silva, Violeta Railean, Aires Duarte, Margarida D. Amaral Published in: Journal of Personalized Medicine, Issue 11/5, 2021, Page(s) 421, ISSN 2075-4426 Publisher: MDPI DOI: 10.3390/jpm11050421 Searching for OpenAIRE data... There was an error trying to search data from OpenAIRE No results available