Project description
Gene therapy for early infantile epileptic encephalopathy
Early infantile epileptic encephalopathy is a rare and severe form of encephalopathy characterised by seizures as well as the absence of language development and walking acquisition. The condition is associated with the WW domain containing the oxidoreductase (WWOX) gene and is thus also known as WWOX‐related epileptic encephalopathy (WOREE). Considering that WOREE infants have a high chance of dying prematurely, the EU-funded WWOXAID project is working on a gene therapy strategy for this syndrome. During the project, researchers will generate and validate the necessary vectors and work towards a business development plan that will bring this promising treatment to the clinic.
Fields of science
Programme(s)
Funding Scheme
ERC-POC-LS - ERC Proof of Concept Lump Sum PilotHost institution
THE HEBREW UNIVERSITY OF JERUSALEM
Net EU contribution
€ 150 000,00
Address
Edmond J Safra Campus Givat Ram
91904 Jerusalem
Israel
91904 Jerusalem
Israel
See on map
Activity type
Higher or Secondary Education Establishments
Non-EU contribution
No data
Beneficiaries (1)
THE HEBREW UNIVERSITY OF JERUSALEM
Israel
Net EU contribution
€ 150 000,00
Address
Edmond J Safra Campus Givat Ram
91904 Jerusalem
91904 Jerusalem
See on map
Activity type
Higher or Secondary Education Establishments
Non-EU contribution
No data