Transplanted human cones incorporate into the retina and function in a murine cone degeneration model
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Autores:
Sylvia J. Gasparini,1 Karen Tessmer,1 Miriam Reh,2 Stephanie Wieneke,1,3 Madalena Carido,1 Manuela Völkner,1,3 Oliver Borsch,1 Anka Swiersy,1 Marta Zuzic,1,4 Olivier Goureau,5 Thomas Kurth,6 Volker Busskamp,1,4 Günther Zeck,2,7 Mike O. Karl,1,3 and Marius Ader1
Publicado en:
J Clin Invest, Edición 2022 Jun 15;132(12):e154619, 2022, ISSN 0021-9738
Editor:
American Society for Clinical Investigation
DOI:
10.1172/jci154619
Neuronal Cell-type Engineering by Transcriptional Activation
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Autores:
Songlei Liu, Johannes Striebel, Giovanni Pasquini, Alex H M Ng, Parastoo Khoshakhlagh , George M Church, Volker Busskamp
Publicado en:
Front Genome Ed ., Edición 16624548, 2021, ISSN 1662-4548
Editor:
Frontiers Research Foundation
DOI:
10.3389/fgeed.2021.715697
Gene-independent therapeutic interventions to maintain and restore light sensitivity in degenerating photoreceptors
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Autores:
Marta Zuzic
Johannes Striebel
Julia S.Pawlick
Kritika Sharma
Frank G.Holz
Volker Busskamp
Publicado en:
Gene-independent therapeutic interventions to maintain and restore light sensitivity in degenerating photoreceptors, 2022, ISSN 1350-9462
Editor:
Pergamon Press Ltd.
DOI:
10.1016/j.preteyeres.2022.101065