Transplanted human cones incorporate into the retina and function in a murine cone degeneration model
(si apre in una nuova finestra)
Autori:
Sylvia J. Gasparini,1 Karen Tessmer,1 Miriam Reh,2 Stephanie Wieneke,1,3 Madalena Carido,1 Manuela Völkner,1,3 Oliver Borsch,1 Anka Swiersy,1 Marta Zuzic,1,4 Olivier Goureau,5 Thomas Kurth,6 Volker Busskamp,1,4 Günther Zeck,2,7 Mike O. Karl,1,3 and Marius Ader1
Pubblicato in:
J Clin Invest, Numero 2022 Jun 15;132(12):e154619, 2022, ISSN 0021-9738
Editore:
American Society for Clinical Investigation
DOI:
10.1172/jci154619
Neuronal Cell-type Engineering by Transcriptional Activation
(si apre in una nuova finestra)
Autori:
Songlei Liu, Johannes Striebel, Giovanni Pasquini, Alex H M Ng, Parastoo Khoshakhlagh , George M Church, Volker Busskamp
Pubblicato in:
Front Genome Ed ., Numero 16624548, 2021, ISSN 1662-4548
Editore:
Frontiers Research Foundation
DOI:
10.3389/fgeed.2021.715697
Gene-independent therapeutic interventions to maintain and restore light sensitivity in degenerating photoreceptors
(si apre in una nuova finestra)
Autori:
Marta Zuzic
Johannes Striebel
Julia S.Pawlick
Kritika Sharma
Frank G.Holz
Volker Busskamp
Pubblicato in:
Gene-independent therapeutic interventions to maintain and restore light sensitivity in degenerating photoreceptors, 2022, ISSN 1350-9462
Editore:
Pergamon Press Ltd.
DOI:
10.1016/j.preteyeres.2022.101065