The importance of international collaboration for rare diseases research: a European perspective
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Autori:
D Julkowska, C P Austin, C M Cutillo, D Gancberg, C Hager, J Halftermeyer, A H Jonker, L P L Lau, I Norstedt, A Rath, R Schuster, E Simelyte, S van Weely
Pubblicato in:
Gene Therapy, Numero 24/9, 2017, Pagina/e 562-571, ISSN 0969-7128
Editore:
Nature Publishing Group
DOI:
10.1038/gt.2017.29
Future of Rare Diseases Research 2017-2027: An IRDiRC Perspective
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Autori:
Christopher P. Austin, Christine M. Cutillo, Lilian P.L. Lau, Anneliene H. Jonker, Ana Rath, Daria Julkowska, David Thomson, Sharon F. Terry, Béatrice de Montleau, Diego Ardigò, Virginie Hivert, Kym M. Boycott, Gareth Baynam, Petra Kaufmann, Domenica Taruscio, Hanns Lochmüller, Makoto Suematsu, Carlo Incerti, Ruxandra Draghia-Akli, Irene Norstedt, Lu Wang, Hugh J.S. Dawkins
Pubblicato in:
Clinical and Translational Science, Numero 11/1, 2018, Pagina/e 21-27, ISSN 1752-8054
Editore:
Wiley-Blackwell
DOI:
10.1111/cts.12500