Publications Peer reviewed articles (2) Lentiviral correction of enzymatic activity restrains macrophage inflammation in adenosine deaminase 2 deficiency Author(s): Matteo Zoccolillo, Immacolata Brigida, Federica Barzaghi, Serena Scala, Raisa Jofra Hernández, Luca Basso-Ricci, Mariasilvia Colantuoni, Emanuela Pettinato, Lucia Sergi Sergi, Giulia Milardi, Paola Capasso, Angelo Lombardo, Silvia Gregori, Francesca Sanvito, Francesca Schena, Simone Cesaro, Francesca Conti, Andrea Pession, Fabio Benedetti, Marco Gattorno, Pui Y. Lee, Luigi Naldini, Maria Pia Cica Published in: Blood Advances, Issue 5/16, 2021, Page(s) 3174-3187, ISSN 2473-9529 Publisher: The American Society of Hematology DOI: 10.1182/bloodadvances.2020003811 Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases Author(s): Francesca Tucci, Samantha Scaramuzza, Alessandro Aiuti, Alessandra Mortellaro Published in: Molecular Therapy, Issue 29/2, 2021, Page(s) 489-504, ISSN 1525-0016 Publisher: Nature Publishing Group DOI: 10.1016/j.ymthe.2020.11.020 Searching for OpenAIRE data... There was an error trying to search data from OpenAIRE No results available