Publikacje Peer reviewed articles (10) Transcriptomic profile of cystic fibrosis patients identifies type I interferon response and ribosomal stalk proteins as potential modifiers of disease severity Autorzy: Michael S. D. Kormann, Alexander Dewerth, Felizitas Eichner, Praveen Baskaran, Andreas Hector, Nicolas Regamey, Dominik Hartl, Rupert Handgretinger, Justin S. Antony Opublikowane w: PLOS ONE, Issue 12/8, 2017, Page(s) e0183526, ISSN 1932-6203 Wydawca: Public Library of Science DOI: 10.1371/journal.pone.0183526 The Oral and Craniofacial Relevance of Chemically Modified RNA Therapeutics Autorzy: Satheesh Elangovan,corresponding author1 Michael S.D. Kormann,2 Behnoush Khorsand,3 and Aliasger K. Salemcorresponding author1,3 Opublikowane w: Discovery Medicine, 2016, ISSN 1539-6509 Wydawca: Discovery Medicine Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis Autorzy: A. K. M. Ashiqul Haque, Alexander Dewerth, Justin S. Antony, Joachim Riethmüller, Georg R. Schweizer, Petra Weinmann, Ngadhnjim Latifi, Hanzey Yasar, Nicoletta Pedemonte, Elvira Sondo, Brian Weidensee, Anjali Ralhan, Julie Laval, Patrick Schlegel, Christian Seitz, Brigitta Loretz, Claus-Michael Lehr, Rupert Handgretinger, Michael S. D. Kormann Opublikowane w: Scientific Reports, Issue 8/1, 2018, ISSN 2045-2322 Wydawca: Nature Publishing Group DOI: 10.1038/s41598-018-34960-0 Recent Developments in mRNA-Based Protein Supplementation Therapy to Target Lung Diseases Autorzy: Itishri Sahu, A.K.M. Ashiqul Haque, Brian Weidensee, Petra Weinmann, Michael S.D. Kormann Opublikowane w: Molecular Therapy, Issue 27/4, 2019, Page(s) 803-823, ISSN 1525-0016 Wydawca: Nature Publishing Group DOI: 10.1016/j.ymthe.2019.02.019 Gene correction of HBB mutations in CD34+ hematopoietic stem cells using Cas9 mRNA and ssODN donors Autorzy: Justin S. Antony, Ngadhnjim Latifi, A. K. M. Ashiqul Haque, Andrés Lamsfus-Calle, Alberto Daniel-Moreno, Sebastian Graeter, Praveen Baskaran, Petra Weinmann, Markus Mezger, Rupert Handgretinger, Michael S. D. Kormann Opublikowane w: Molecular and Cellular Pediatrics, Issue 5/1, 2018, ISSN 2194-7791 Wydawca: Springer Open DOI: 10.1186/s40348-018-0086-1 Uridine Depletion and Chemical Modification Increase Cas9 mRNA Activity and Reduce Immunogenicity without HPLC Purification Autorzy: Sriram Vaidyanathan, Krist T. Azizian, A.K.M. Ashiqul Haque, Jordana M. Henderson, Ayal Hendel, Sabrina Shore, Justin S. Antony, Richard I. Hogrefe, Michael S.D. Kormann, Matthew H. Porteus, Anton P. McCaffrey Opublikowane w: Molecular Therapy - Nucleic Acids, Issue 12, 2018, Page(s) 530-542, ISSN 2162-2531 Wydawca: Nature Publishing Group DOI: 10.1016/j.omtn.2018.06.010 RNA ImmunoGenic Assay: Simple method for detecting immunogenicity of in vitro transcribed mRNA Autorzy: AKM Ashiqul Haque, Petra Weinmann, Sumit Biswas, Rupert Handgretinger, Markus Mezger, Michael S. D. Kormann, Justin S. Antony Opublikowane w: ADVANCES IN CELL AND GENE THERAPY, Issue 3/2, 2020, ISSN 2573-8461 Wydawca: John Wiley & Sons Ltd. DOI: 10.1002/acg2.79 Modified mRNA as a new therapeutic option for pediatric respiratory diseases and hemoglobinopathies Autorzy: Justin S. Antony, Alexander Dewerth, Ashiqul Haque, Rupert Handgretinger, Michael S.D. Kormann Opublikowane w: Molecular and Cellular Pediatrics, Issue 2/1, 2015, ISSN 2194-7791 Wydawca: SpringerOpen DOI: 10.1186/s40348-015-0022-6 mRNA-Mediated Gene Supplementation of Toll-Like Receptors as Treatment Strategy for Asthma In Vivo Autorzy: Franziska Zeyer, Benedikt Mothes, Clara Will, Melanie Carevic, Jennifer Rottenberger, Bernd Nürnberg, Dominik Hartl, Rupert Handgretinger, Sandra Beer-Hammer, Michael S. D. Kormann Opublikowane w: PLOS ONE, Issue 11/4, 2016, Page(s) e0154001, ISSN 1932-6203 Wydawca: Public Library of Science DOI: 10.1371/journal.pone.0154001 In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency Autorzy: Azita J Mahiny, Alexander Dewerth, Lauren E Mays, Mohammed Alkhaled, Benedikt Mothes, Emad Malaeksefat, Brigitta Loretz, Jennifer Rottenberger, Darina M Brosch, Philipp Reautschnig, Pacharapan Surapolchai, Franziska Zeyer, Andrea Schams, Melanie Carevic, Martina Bakele, Matthias Griese, Matthias Schwab, Bernd Nürnberg, Sandra Beer-Hammer, Rupert Handgretinger, Dominik Hartl, Claus-Michael Lehr, M Opublikowane w: Nature Biotechnology, 2015, ISSN 1087-0156 Wydawca: Nature Publishing Group DOI: 10.1038/nbt.3241 Wyszukiwanie danych OpenAIRE... Podczas wyszukiwania danych OpenAIRE wystąpił błąd Brak wyników