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Intra Erythrocyte Dexamethasone in the treatment of Ataxia Telangiectasia

Rezultaty

First evaluation workshop
Report on AT NEST definition, guidelines and SOPs
Registration number of clinical study in approved registry

Registration number of clinical study in approved registry Informed Consents Forms and/or Data Protection Forms (in their final version) will be included here. The authorisation for the use of personal data for specified purposes for a specified duration, and if applicable data transfers to third countries will be part of the content of these forms. Mandatory deliverable

Statistical report of comparison
Final evaluation workshop

Publikacje

DDIT4 gene expression is switched on by a new HDAC4 function in ataxia telangiectasia

Autorzy: Anastasia Ricci, Luca Galluzzi, Mauro Magnani, Michele Menotta
Opublikowane w: The FASEB Journal, Numer 34/1, 2020, Strona(/y) 1802-1818, ISSN 0892-6638
Wydawca: Federation of American Societies for Experimental Biology
DOI: 10.1096/fj.201902039r

The nucleoplasmic interactions among Lamin A/C-pRB-LAP2α-E2F1 are modulated by dexamethasone

Autorzy: Anastasia Ricci, Sara Orazi, Federica Biancucci, Mauro Magnani, Michele Menotta
Opublikowane w: Scientific Reports, Numer 11/1, 2021, ISSN 2045-2322
Wydawca: Nature Publishing Group
DOI: 10.1038/s41598-021-89608-3

Proteomics and transcriptomics analyses of ataxia telangiectasia cells treated with Dexamethasone

Autorzy: Michele Menotta, Sara Orazi, Anna Maria Gioacchini, Chiara Spapperi, Anastasia Ricci, Luciana Chessa, Mauro Magnani
Opublikowane w: PLOS ONE, Numer 13/4, 2018, Strona(/y) e0195388, ISSN 1932-6203
Wydawca: Public Library of Science
DOI: 10.1371/journal.pone.0195388

ATM splicing variants as biomarkers for low dose dexamethasone treatment of A-T

Autorzy: Michele Menotta, Sara Biagiotti, Chiara Spapperi, Sara Orazi, Luigia Rossi, Luciana Chessa, Vincenzo Leuzzi, Daniela D’Agnano, Annarosa Soresina, Roberto Micheli, Mauro Magnani
Opublikowane w: Orphanet Journal of Rare Diseases, Numer 12/1, 2017, ISSN 1750-1172
Wydawca: BioMed Central
DOI: 10.1186/s13023-017-0669-2

Ex vivo encapsulation of dexamethasone sodium phosphate into human autologous erythrocytes using fully automated biomedical equipment

Autorzy: Giovanni Mambrini, Marco Mandolini, Luigia Rossi, Francesca Pierigè, Giovanni Capogrossi, Patricia Salvati, Sonja Serafini, Luca Benatti, Mauro Magnani
Opublikowane w: International Journal of Pharmaceutics, Numer 517/1-2, 2017, Strona(/y) 175-184, ISSN 0378-5173
Wydawca: Elsevier BV
DOI: 10.1016/j.ijpharm.2016.12.011

In vivo effects of dexamethasone on blood gene expression in ataxia telangiectasia

Autorzy: Michele Menotta, Sara Biagiotti, Sara Orazi, Luigia Rossi, Luciana Chessa, Vincenzo Leuzzi, Daniela D’Agnano, Alessandro Plebani, Annarosa Soresina, Mauro Magnani
Opublikowane w: Molecular and Cellular Biochemistry, Numer 438/1-2, 2018, Strona(/y) 153-166, ISSN 0300-8177
Wydawca: Kluwer Academic/Plenum Publishers
DOI: 10.1007/s11010-017-3122-x

Transcriptomic profile of ataxia telangiectasia cells treated for 30 days with a low dose of dexamethasone

Autorzy: Anastasia Ricci, Federica Biancucci, Mauro Magnani, Michele Menotta
Opublikowane w: All Life, Numer 14/1, 2021, Strona(/y) 277-286, ISSN 2689-5293
Wydawca: all life
DOI: 10.1080/26895293.2021.1911863

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